List of Current Trials
ALS Imaging
- Investigator
- James Wymer
- Location
- Gainesville
ARTHREX
The goal of this clinical trial is to test ATX-01 in participants with myotonic dystrophy type 1 (DM1). The main question it aims to answer is if ATX-01 is…
- Investigator
- Sankarasubramoney Subramony
- Protocol ID
- NCT06300307
- Ages
- 18 Years – 64 Years
- Sexes
- All
- Location
- Gainesville
Avidity FSHD
A Randomized, Double-blind, Placebo-controlled, Phase 1/2 Study to Evaluate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics, and Exploratory…
- Investigator
- Sankarasubramoney Subramony
- Protocol ID
- NCT05747924
- Ages
- 16 Years – 70 Years
- Sexes
- All
- Location
- Gainesville
COYA
The ALSTARS trial will be conducted across 20-25 sites in the US and Canada, and will evaluate the safety and efficacy of an investigational treatment called…
- Investigator
- James Wymer
- Protocol ID
- NCT07161999
- Ages
- 18 Years – 80 Years
- Sexes
- All
- Location
- Gainesville
Fortitude OLE (AOC 1020-CS2)
A Phase 2 Open-label Extension Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of AOC 1020 Administered Intravenously to Participants with…
- Investigator
- Sankarasubramoney Subramony
- Protocol ID
- NCT06547216
- Ages
- 16 Years – 72 Years
- Sexes
- All
- Location
- Gainesville
HARBOR
A Phase 3 Randomized, Double-Blind, Placebo-Controlled, Global Study to Evaluate the Efficacy and Safety of Intravenous Delpacibart Etedesiran (abbreviated…
- Investigator
- Sankarasubramoney Subramony
- Protocol ID
- NCT06411288
- Ages
- 16 Years – 65 Years
- Sexes
- All
- Location
- Gainesville
HEALEY ALS Platform Trial
The HEALEY ALS Platform Trial is a perpetual multi-center, multi-regimen clinical trial evaluating the safety and efficacy of investigational products for the…
- Investigator
- James Wymer
- Protocol ID
- NCT04297683
- Ages
- 18 Years – N/A
- Sexes
- All
- Location
- Gainesville
LUMINA
This study is a placebo-controlled Phase I study to evaluate the safety, tolerability, pharmacokinetics, and pharmacodynamics of the antisense oligonucleotide…
- Investigator
- James Wymer
- Protocol ID
- NCT06665165
- Ages
- 18 Years – N/A
- Sexes
- All
- Location
- Gainesville
Motor Outcomes to Validate Evaluations in FSHD (MOVE FSHD)
- Investigator
- Sankarasubramoney Subramony
- Location
- Gainesville
PASS
In this study, researchers will learn more about the safety of BIIB141, also known as omaveloxolone or SKYCLARYS®. This is a drug available for doctors to…
- Investigator
- Sankarasubramoney Subramony
- Protocol ID
- NCT06623890
- Ages
- 16 Years – N/A
- Sexes
- All
- Location
- Gainesville